JPWO2022231950A5 - - Google Patents

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Publication number
JPWO2022231950A5
JPWO2022231950A5 JP2023566490A JP2023566490A JPWO2022231950A5 JP WO2022231950 A5 JPWO2022231950 A5 JP WO2022231950A5 JP 2023566490 A JP2023566490 A JP 2023566490A JP 2023566490 A JP2023566490 A JP 2023566490A JP WO2022231950 A5 JPWO2022231950 A5 JP WO2022231950A5
Authority
JP
Japan
Prior art keywords
pharmaceutical composition
nucleic acid
seq
ngly1
nucleotide sequence
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2023566490A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024517737A5 (https=
JP2024517737A (ja
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/025834 external-priority patent/WO2022231950A1/en
Publication of JP2024517737A publication Critical patent/JP2024517737A/ja
Publication of JP2024517737A5 publication Critical patent/JP2024517737A5/ja
Publication of JPWO2022231950A5 publication Critical patent/JPWO2022231950A5/ja
Pending legal-status Critical Current

Links

JP2023566490A 2021-04-26 2022-04-21 Ｎｇｙｌ１欠損症を治療する組成物及び方法 Pending JP2024517737A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202163180065P 2021-04-26 2021-04-26
US63/180,065 2021-04-26
PCT/US2022/025834 WO2022231950A1 (en) 2021-04-26 2022-04-21 Compositions and methods for treating ngyl1 deficiency

Publications (3)

Publication Number Publication Date
JP2024517737A JP2024517737A (ja) 2024-04-23
JP2024517737A5 JP2024517737A5 (https=) 2025-06-02
JPWO2022231950A5 true JPWO2022231950A5 (https=) 2025-06-02

Family

ID=83848571

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023566490A Pending JP2024517737A (ja) 2021-04-26 2022-04-21 Ｎｇｙｌ１欠損症を治療する組成物及び方法

Country Status (5)

Country Link
US (1) US20240218396A1 (https=)
EP (1) EP4329824A4 (https=)
JP (1) JP2024517737A (https=)
CA (1) CA3216809A1 (https=)
WO (1) WO2022231950A1 (https=)

Family Cites Families (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
IL248102B (en) * 2014-05-02 2022-07-01 Genzyme Corp aav vectors for gene therapy of the central nervous system and retina
EP3564263A1 (en) * 2018-05-03 2019-11-06 Universitätsklinikum Hamburg-Eppendorf Fusion proteins comprising a cell surface marker specific vhh
WO2020210592A1 (en) * 2019-04-12 2020-10-15 University Of Massachusetts Recombinant aav gene therapy for ngyl1 deficiency

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