JPWO2022156378A5 - - Google Patents
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- JPWO2022156378A5 JPWO2022156378A5 JP2023541700A JP2023541700A JPWO2022156378A5 JP WO2022156378 A5 JPWO2022156378 A5 JP WO2022156378A5 JP 2023541700 A JP2023541700 A JP 2023541700A JP 2023541700 A JP2023541700 A JP 2023541700A JP WO2022156378 A5 JPWO2022156378 A5 JP WO2022156378A5
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- interspersed element
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- 239000013598 vector Substances 0.000 claims 38
- 108090000623 proteins and genes Proteins 0.000 claims 28
- 108091026890 Coding region Proteins 0.000 claims 24
- 238000013518 transcription Methods 0.000 claims 24
- 230000035897 transcription Effects 0.000 claims 24
- 101710158030 Endonuclease Proteins 0.000 claims 18
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- 208000007641 Pinealoma Diseases 0.000 claims 2
- 102000017143 RNA Polymerase I Human genes 0.000 claims 2
- 108010013845 RNA Polymerase I Proteins 0.000 claims 2
- 102000009572 RNA Polymerase II Human genes 0.000 claims 2
- 108010009460 RNA Polymerase II Proteins 0.000 claims 2
- 102000014450 RNA Polymerase III Human genes 0.000 claims 2
- 108010078067 RNA Polymerase III Proteins 0.000 claims 2
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- 102000014461 Ataxins Human genes 0.000 claims 1
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- 206010008025 Cerebellar ataxia Diseases 0.000 claims 1
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- 206010009944 Colon cancer Diseases 0.000 claims 1
- 208000006992 Color Vision Defects Diseases 0.000 claims 1
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- 208000009415 Spinocerebellar Ataxias Diseases 0.000 claims 1
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- 208000002903 Thalassemia Diseases 0.000 claims 1
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- 208000006105 Uterine Cervical Neoplasms Diseases 0.000 claims 1
- 208000002495 Uterine Neoplasms Diseases 0.000 claims 1
- 208000014070 Vestibular schwannoma Diseases 0.000 claims 1
- 201000006035 X-linked dominant hypophosphatemic rickets Diseases 0.000 claims 1
- 208000008919 achondroplasia Diseases 0.000 claims 1
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- 239000003814 drug Substances 0.000 claims 1
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- 210000001519 tissue Anatomy 0.000 claims 1
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- 208000032349 type 2B vitamin D-dependent rickets Diseases 0.000 claims 1
- 206010046766 uterine cancer Diseases 0.000 claims 1
- 239000013603 viral vector Substances 0.000 claims 1
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| CN202110089068.1A CN112708636A (zh) | 2021-01-22 | 2021-01-22 | 基因转录框架、载体系统、基因组序列编辑方法及应用 |
| CN202110089068.1 | 2021-01-22 | ||
| PCT/CN2021/134710 WO2022156378A1 (zh) | 2021-01-22 | 2021-12-01 | 基因转录框架、载体系统、基因组序列编辑方法及应用 |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2024504592A JP2024504592A (ja) | 2024-02-01 |
| JPWO2022156378A5 true JPWO2022156378A5 (https=) | 2024-12-10 |
| JP2024504592A5 JP2024504592A5 (https=) | 2024-12-10 |
Family
ID=75550451
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023541700A Pending JP2024504592A (ja) | 2021-01-22 | 2021-12-01 | 遺伝子転写フレームワーク、ベクターシステム、ゲノム配列編集方法および応用 |
Country Status (11)
| Country | Link |
|---|---|
| US (1) | US20250263737A1 (https=) |
| EP (1) | EP4282968A4 (https=) |
| JP (1) | JP2024504592A (https=) |
| KR (1) | KR20230135630A (https=) |
| CN (1) | CN112708636A (https=) |
| AU (1) | AU2021422067A1 (https=) |
| BR (1) | BR112023014382A2 (https=) |
| CA (1) | CA3206081A1 (https=) |
| MX (1) | MX2023008635A (https=) |
| WO (1) | WO2022156378A1 (https=) |
| ZA (1) | ZA202308025B (https=) |
Families Citing this family (3)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| CN112481259B (zh) * | 2020-11-24 | 2022-09-16 | 南昌大学 | 两种甘薯U6基因启动子IbU6的克隆与应用 |
| CN115044583A (zh) * | 2022-03-21 | 2022-09-13 | 隋云鹏 | 用于基因编辑的rna框架和基因编辑方法 |
| CN115312121B (zh) * | 2022-09-29 | 2023-03-24 | 北京齐碳科技有限公司 | 靶基因位点检测方法、装置、设备及计算机存储介质 |
Family Cites Families (8)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| EP2281050B1 (en) * | 2008-04-14 | 2014-04-02 | Sangamo BioSciences, Inc. | Linear donor constructs for targeted integration |
| CN102080101B (zh) * | 2010-11-25 | 2013-01-09 | 北京济福霖生物技术有限公司 | 一种定点整合外源基因的方法 |
| WO2016030501A1 (en) * | 2014-08-28 | 2016-03-03 | Centre National De La Recherche Scientifique - Cnrs - | Synthetic alu-retrotransposon vectors for gene therapy |
| US11339427B2 (en) * | 2016-02-12 | 2022-05-24 | Jumpcode Genomics, Inc. | Method for target specific RNA transcription of DNA sequences |
| CN113286880A (zh) * | 2018-08-28 | 2021-08-20 | 旗舰先锋创新Vi有限责任公司 | 调控基因组的方法和组合物 |
| US20210340562A1 (en) * | 2018-10-19 | 2021-11-04 | Board Of Regents, The University Of Texas System | Engineered long interspersed element (line) transposons and methods of use |
| JP7831937B2 (ja) * | 2019-09-03 | 2026-03-17 | クリエイト・メディシンズ，インコーポレーテッド | ゲノム組込みのための方法および組成物 |
| CN112210573B (zh) * | 2020-10-14 | 2024-02-06 | 浙江大学 | 一种用基因编辑改造原代细胞的dna模板及定点插入方法 |
-
2021
- 2021-01-22 CN CN202110089068.1A patent/CN112708636A/zh active Pending
- 2021-12-01 JP JP2023541700A patent/JP2024504592A/ja active Pending
- 2021-12-01 US US18/266,592 patent/US20250263737A1/en active Pending
- 2021-12-01 AU AU2021422067A patent/AU2021422067A1/en active Pending
- 2021-12-01 BR BR112023014382A patent/BR112023014382A2/pt unknown
- 2021-12-01 EP EP21920753.7A patent/EP4282968A4/en active Pending
- 2021-12-01 CA CA3206081A patent/CA3206081A1/en active Pending
- 2021-12-01 WO PCT/CN2021/134710 patent/WO2022156378A1/zh not_active Ceased
- 2021-12-01 MX MX2023008635A patent/MX2023008635A/es unknown
- 2021-12-01 KR KR1020237028513A patent/KR20230135630A/ko active Pending
-
2023
- 2023-08-18 ZA ZA2023/08025A patent/ZA202308025B/en unknown
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