JPWO2022011156A5 - - Google Patents

Download PDF

Info

Publication number
JPWO2022011156A5
JPWO2022011156A5 JP2023501477A JP2023501477A JPWO2022011156A5 JP WO2022011156 A5 JPWO2022011156 A5 JP WO2022011156A5 JP 2023501477 A JP2023501477 A JP 2023501477A JP 2023501477 A JP2023501477 A JP 2023501477A JP WO2022011156 A5 JPWO2022011156 A5 JP WO2022011156A5
Authority
JP
Japan
Prior art keywords
mol
lipid
formulation
nucleic acid
cationic lipid
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2023501477A
Other languages
English (en)
Japanese (ja)
Other versions
JP2023534206A5 (https=
JP2023534206A (ja
Publication date
Application filed filed Critical
Priority claimed from PCT/US2021/040913 external-priority patent/WO2022011156A1/en
Publication of JP2023534206A publication Critical patent/JP2023534206A/ja
Publication of JP2023534206A5 publication Critical patent/JP2023534206A5/ja
Publication of JPWO2022011156A5 publication Critical patent/JPWO2022011156A5/ja
Pending legal-status Critical Current

Links

JP2023501477A 2020-07-10 2021-07-08 肺に治療薬を送達するための脂質ナノ粒子 Pending JP2023534206A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202063050594P 2020-07-10 2020-07-10
US63/050,594 2020-07-10
PCT/US2021/040913 WO2022011156A1 (en) 2020-07-10 2021-07-08 Lipid nanoparticles for delivering therapeutics to lungs

Publications (3)

Publication Number Publication Date
JP2023534206A JP2023534206A (ja) 2023-08-08
JP2023534206A5 JP2023534206A5 (https=) 2024-07-03
JPWO2022011156A5 true JPWO2022011156A5 (https=) 2024-07-03

Family

ID=79552114

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023501477A Pending JP2023534206A (ja) 2020-07-10 2021-07-08 肺に治療薬を送達するための脂質ナノ粒子

Country Status (10)

Country Link
US (1) US20240065982A1 (https=)
EP (1) EP4178585A4 (https=)
JP (1) JP2023534206A (https=)
KR (1) KR20230038217A (https=)
CN (1) CN115768438A (https=)
AU (1) AU2021305214A1 (https=)
CA (1) CA3188661A1 (https=)
IL (1) IL299750A (https=)
MX (1) MX2023000511A (https=)
WO (1) WO2022011156A1 (https=)

Families Citing this family (9)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
MX2021005462A (es) * 2018-11-09 2021-08-24 Arbutus Biopharma Corp Lipidos cationicos que contienen silicio.
CZ310613B6 (cs) 2020-09-23 2026-01-28 Ústav organické chemie a biochemie AV ČR, v. v. i. Lipidoidy pro transfekci nukleových kyselin a jejich použití
CZ310443B6 (cs) 2021-07-19 2025-06-25 Ústav organické chemie a biochemie AV ČR, v. v. i. Cyklohexanové lipidoidy pro transfekci nukleových kyselin a jejich použití
CN119654166A (zh) 2022-04-01 2025-03-18 内诺维什疗法股份有限公司 mRNA递送方法及其组合物
KR20250094676A (ko) * 2022-10-25 2025-06-25 나노베이션 테라퓨틱스 인크. 안티-센스 올리고뉴클레오티드 전달을 위한 지질 나노입자 제형
WO2025133951A1 (en) * 2023-12-21 2025-06-26 Genevant Sciences Gmbh Ionizable lipids suitable for lipid nanoparticles
WO2025166323A2 (en) 2024-02-02 2025-08-07 Editas Medicine, Inc. Crispr-related methods and compositions targeting lipoprotein (a) expression
WO2025213138A1 (en) 2024-04-05 2025-10-09 Editas Medicine, Inc. Crispr/rna-guided nuclease related methods and compositions for treating primary open angle glaucoma
CN118576568B (zh) * 2024-08-06 2024-11-26 北京悦康科创医药科技股份有限公司 一种药物组合物及其制备方法和应用

Family Cites Families (6)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
AU2009238175C1 (en) * 2008-04-15 2023-11-30 Arbutus Biopharma Corporation Novel lipid formulations for nucleic acid delivery
EP3319976B1 (en) * 2015-07-09 2021-09-01 Insmed Incorporated Compositions and methods for treating lung diseases and lung injury
CA3103528A1 (en) * 2018-06-19 2019-12-26 The Board Of Regents Of The University Of Texas System Lipid nanoparticle compositions for delivery of mrna and long nucleic acids
DE102018127300A1 (de) * 2018-10-31 2020-04-30 Henkel Ag & Co. Kgaa Wirkstoffzusammensetzung zum Schutz künstlich gefärbter Haare
MX2021005462A (es) * 2018-11-09 2021-08-24 Arbutus Biopharma Corp Lipidos cationicos que contienen silicio.
AU2020262437A1 (en) * 2019-04-26 2021-12-23 Genevant Sciences Gmbh Lipid nanoparticles

Similar Documents

Publication Publication Date Title
US9080186B2 (en) Compositions comprising cationic amphiphiles and colipids for delivering therapeutic molecules
EP2395012B1 (en) Modified siRNA molecules and uses thereof
EP2567693B1 (en) Lipid encapsulated interfering RNA
US20070218122A1 (en) siRNA silencing of influenza virus gene expression
CN115708818B (zh) 一种用于雾化吸入脂质纳米粒的通用型处方
TW202539707A (zh) 用於治療b型肝炎之治療組成物及方法
CN118634207B (zh) 一种雾化吸入用核酸-脂质纳米粒及其制备方法和应用
TW201735950A (zh) 用於治療b型肝炎之治療組合物及方法
JPWO2022011156A5 (https=)
JPWO2020097520A5 (https=)
JPWO2023144798A5 (https=)
TW202603166A (zh) 黏蛋白5B(MUC5B)靶向siRNA及反義寡核苷酸及其使用方法
CN119424366A (zh) 靶向次级淋巴器官的脂质纳米颗粒及其制备方法和用途
HK1123751B (en) Lipid encapsulated interfering rna