JPWO2021258011A5 - - Google Patents

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Publication number
JPWO2021258011A5
JPWO2021258011A5 JP2022570473A JP2022570473A JPWO2021258011A5 JP WO2021258011 A5 JPWO2021258011 A5 JP WO2021258011A5 JP 2022570473 A JP2022570473 A JP 2022570473A JP 2022570473 A JP2022570473 A JP 2022570473A JP WO2021258011 A5 JPWO2021258011 A5 JP WO2021258011A5
Authority
JP
Japan
Prior art keywords
modified oligonucleotide
oligomeric compound
modified
internucleoside linkage
oligomeric
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2022570473A
Other languages
English (en)
Japanese (ja)
Other versions
JP2023530072A (ja
JP2023530072A5 (https=
Publication date
Application filed filed Critical
Priority claimed from PCT/US2021/038126 external-priority patent/WO2021258011A1/en
Publication of JP2023530072A publication Critical patent/JP2023530072A/ja
Publication of JP2023530072A5 publication Critical patent/JP2023530072A5/ja
Publication of JPWO2021258011A5 publication Critical patent/JPWO2021258011A5/ja
Pending legal-status Critical Current

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JP2022570473A 2020-06-19 2021-06-18 Ｐｍｐ２２を調節するための化合物及び方法 Pending JP2023530072A (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US202063041643P 2020-06-19 2020-06-19
US202063041474P 2020-06-19 2020-06-19
US63/041,474 2020-06-19
US63/041,643 2020-06-19
PCT/US2021/038126 WO2021258011A1 (en) 2020-06-19 2021-06-18 Compounds and methods for modulating pmp22

Publications (3)

Publication Number Publication Date
JP2023530072A JP2023530072A (ja) 2023-07-13
JP2023530072A5 JP2023530072A5 (https=) 2024-06-24
JPWO2021258011A5 true JPWO2021258011A5 (https=) 2024-06-24

Family

ID=79025354

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2022570473A Pending JP2023530072A (ja) 2020-06-19 2021-06-18 Ｐｍｐ２２を調節するための化合物及び方法

Country Status (4)

Country Link
US (1) US20230374519A1 (https=)
EP (1) EP4168549A4 (https=)
JP (1) JP2023530072A (https=)
WO (1) WO2021258011A1 (https=)

Families Citing this family (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
AU2017229778A1 (en) 2016-03-09 2018-08-16 Ionis Pharmaceuticals, Inc. Methods and compositions for inhibiting PMP22 expression
WO2025150052A1 (en) * 2024-01-12 2025-07-17 Potentia Ltd. Targeted delivery of drug conjugates to schwann cells and treatment methods in schwann cell-related diseases

Family Cites Families (7)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
KR101869570B1 (ko) * 2010-04-28 2018-06-20 아이오니스 파마수티컬즈, 인코포레이티드 변형된 뉴클레오사이드 및 그로부터 제조된 올리고머 화합물
EP3286318A2 (en) * 2015-04-22 2018-02-28 Mina Therapeutics Limited Sarna compositions and methods of use
AU2017229778A1 (en) * 2016-03-09 2018-08-16 Ionis Pharmaceuticals, Inc. Methods and compositions for inhibiting PMP22 expression
AU2019218987B2 (en) * 2018-02-12 2025-04-24 Ionis Pharmaceuticals, Inc. Modified compounds and uses thereof
EP3628735A1 (en) * 2018-09-25 2020-04-01 Centre National De La Recherche Scientifique Antisense rna targeting pmp22 for the treatment of charcot-marie-tooth 1a disease
WO2020132558A1 (en) * 2018-12-21 2020-06-25 Ionis Pharmaceuticals, Inc. Compounds and methods for reducing pmp22 expression
JP2023501352A (ja) * 2019-11-08 2023-01-18 アイオーニス ファーマシューティカルズ， インコーポレーテッド Ｓｐｄｅｆ発現を低減するための化合物及び方法

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