JPWO2021127455A5 - - Google Patents

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Publication number
JPWO2021127455A5
JPWO2021127455A5 JP2022537012A JP2022537012A JPWO2021127455A5 JP WO2021127455 A5 JPWO2021127455 A5 JP WO2021127455A5 JP 2022537012 A JP2022537012 A JP 2022537012A JP 2022537012 A JP2022537012 A JP 2022537012A JP WO2021127455 A5 JPWO2021127455 A5 JP WO2021127455A5
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JP
Japan
Prior art keywords
nucleic acid
isolated nucleic
composition
raav
subject
Prior art date
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Application number
JP2022537012A
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English (en)
Japanese (ja)
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JP2023507741A5 (https=
JP7730327B2 (ja
JP2023507741A (ja
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Priority claimed from PCT/US2020/066039 external-priority patent/WO2021127455A1/en
Publication of JP2023507741A publication Critical patent/JP2023507741A/ja
Publication of JP2023507741A5 publication Critical patent/JP2023507741A5/ja
Publication of JPWO2021127455A5 publication Critical patent/JPWO2021127455A5/ja
Priority to JP2025135462A priority Critical patent/JP2025166191A/ja
Application granted granted Critical
Publication of JP7730327B2 publication Critical patent/JP7730327B2/ja
Active legal-status Critical Current
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JP2022537012A 2019-12-20 2020-12-18 ハンチントン病を処置するための方法 Active JP7730327B2 (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2025135462A JP2025166191A (ja) 2019-12-20 2025-08-15 ハンチントン病を処置するための方法

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201962951582P 2019-12-20 2019-12-20
US62/951,582 2019-12-20
PCT/US2020/066039 WO2021127455A1 (en) 2019-12-20 2020-12-18 Methods for treating huntington's disease

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2025135462A Division JP2025166191A (ja) 2019-12-20 2025-08-15 ハンチントン病を処置するための方法

Publications (4)

Publication Number Publication Date
JP2023507741A JP2023507741A (ja) 2023-02-27
JP2023507741A5 JP2023507741A5 (https=) 2023-12-06
JPWO2021127455A5 true JPWO2021127455A5 (https=) 2023-12-06
JP7730327B2 JP7730327B2 (ja) 2025-08-27

Family

ID=76478540

Family Applications (2)

Application Number Title Priority Date Filing Date
JP2022537012A Active JP7730327B2 (ja) 2019-12-20 2020-12-18 ハンチントン病を処置するための方法
JP2025135462A Pending JP2025166191A (ja) 2019-12-20 2025-08-15 ハンチントン病を処置するための方法

Family Applications After (1)

Application Number Title Priority Date Filing Date
JP2025135462A Pending JP2025166191A (ja) 2019-12-20 2025-08-15 ハンチントン病を処置するための方法

Country Status (7)

Country Link
US (1) US20230340470A1 (https=)
EP (1) EP4076656A4 (https=)
JP (2) JP7730327B2 (https=)
CN (1) CN115443339A (https=)
AU (1) AU2020407119A1 (https=)
CA (1) CA3163034A1 (https=)
WO (1) WO2021127455A1 (https=)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
AU2023211606A1 (en) * 2022-01-27 2024-07-11 AskBio Inc. Compositions for treating neurological disease

Family Cites Families (11)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2003084977A1 (en) * 2002-04-04 2003-10-16 Xiao Xiao Gene expression control system and its use in recombinant virus packaging cell lines
US8795987B2 (en) * 2005-02-11 2014-08-05 International Business Machines Corporation Ribonucleic acid interference molecules of Oryza sativa
WO2007051045A2 (en) * 2005-10-28 2007-05-03 Alnylam Pharmaceuticals, Inc. Compositions and methods for inhibiting expression of huntingtin gene
PT2161038E (pt) * 2006-01-26 2014-03-10 Isis Pharmaceuticals Inc Composições e suas utilizações dirigidas à huntingtina
US9920317B2 (en) * 2010-11-12 2018-03-20 The General Hospital Corporation Polycomb-associated non-coding RNAs
WO2015070212A1 (en) * 2013-11-11 2015-05-14 Sangamo Biosciences, Inc. Methods and compositions for treating huntington's disease
RU2691102C2 (ru) * 2014-05-08 2019-06-11 Сангамо Байосайенсиз, Инк. Способы и композиции для лечения болезни хантингтона
AU2015274457A1 (en) * 2014-06-11 2017-01-05 Circuit Therapeutics, Inc. Optogenetic therapies for movement disorders
US10457940B2 (en) * 2016-09-22 2019-10-29 University Of Massachusetts AAV treatment of Huntington's disease
WO2019217483A1 (en) * 2018-05-07 2019-11-14 Spark Therapeutics, Inc. Plasmid free aav vector producing cell lines
BR112022003505A2 (pt) * 2019-08-27 2022-05-24 Vertex Pharma Composições e métodos para tratamento de distúrbios associados a dna repetitivo

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