JPWO2021058830A5 - - Google Patents
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- Publication number
- JPWO2021058830A5 JPWO2021058830A5 JP2022519283A JP2022519283A JPWO2021058830A5 JP WO2021058830 A5 JPWO2021058830 A5 JP WO2021058830A5 JP 2022519283 A JP2022519283 A JP 2022519283A JP 2022519283 A JP2022519283 A JP 2022519283A JP WO2021058830 A5 JPWO2021058830 A5 JP WO2021058830A5
- Authority
- JP
- Japan
- Prior art keywords
- sequence
- aav vector
- seq
- vector according
- pgrn
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| GB201913974A GB201913974D0 (en) | 2019-09-27 | 2019-09-27 | Vector |
| GB1913974.0 | 2019-09-27 | ||
| PCT/EP2020/077144 WO2021058830A1 (en) | 2019-09-27 | 2020-09-28 | Vector |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2022549892A JP2022549892A (ja) | 2022-11-29 |
| JP2022549892A5 JP2022549892A5 (https=) | 2023-10-12 |
| JPWO2021058830A5 true JPWO2021058830A5 (https=) | 2023-10-12 |
Family
ID=68538788
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022519283A Pending JP2022549892A (ja) | 2019-09-27 | 2020-09-28 | ベクター |
Country Status (8)
| Country | Link |
|---|---|
| US (1) | US20220380804A1 (https=) |
| EP (1) | EP4034664A1 (https=) |
| JP (1) | JP2022549892A (https=) |
| CN (3) | CN119913208A (https=) |
| AU (1) | AU2020354538A1 (https=) |
| CA (1) | CA3155742A1 (https=) |
| GB (1) | GB201913974D0 (https=) |
| WO (1) | WO2021058830A1 (https=) |
Families Citing this family (3)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| CA3228916A1 (en) * | 2021-08-11 | 2023-02-16 | King's College London | Compositions and methods for improved treatment of disorders affecting the central nervous system |
| CN116064624A (zh) * | 2022-09-15 | 2023-05-05 | 思鹏生物科技(苏州)有限公司 | 利用rpl基因促进载体稳定表达的方法及其功能基因 |
| WO2024245120A1 (en) * | 2023-05-26 | 2024-12-05 | Shanghai Vitalgen Biopharma Co., Ltd. | Recombinant aav vectors for treating proteinopathies in central nervous system |
Family Cites Families (20)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| EP0173552B1 (en) | 1984-08-24 | 1991-10-09 | The Upjohn Company | Recombinant dna compounds and the expression of polypeptides such as tpa |
| CA2265460A1 (en) | 1996-09-11 | 1998-03-19 | The Government Of The United States Of America, Represented By The Secre Tary, Department Of Health And Human Services | Aav4 vector and uses thereof |
| US6083725A (en) * | 1996-09-13 | 2000-07-04 | Transkaryotic Therapies, Inc. | Tranfected human cells expressing human α-galactosidase A protein |
| US6156303A (en) | 1997-06-11 | 2000-12-05 | University Of Washington | Adeno-associated virus (AAV) isolates and AAV vectors derived therefrom |
| EP1082413B1 (en) | 1998-05-28 | 2008-07-23 | THE GOVERNMENT OF THE UNITED STATES OF AMERICA, as represented by THE SECRETARY, DEPARTMENT OF HEALTH AND HUMAN SERVICES | Aav5 vector and uses thereof |
| CA2349838C (en) | 1998-11-05 | 2011-06-07 | The Trustees Of The University Of Pennsylvania | Adeno-associated virus serotype 1 nucleic acid sequences, vectors and host cells containing same |
| US7071172B2 (en) * | 2002-04-30 | 2006-07-04 | The University Of North Carolina At Chapel Hill | Secretion signal vectors |
| CA2653974A1 (en) * | 2006-05-30 | 2008-02-14 | Mayo Foundation For Medical Education And Research | Detecting and treating dementia |
| HRP20171334T1 (hr) | 2011-04-22 | 2017-11-17 | The Regents Of The University Of California | Virioni adeno-povezanog virusa s kapsid varijantom i postupci njihove upotrebe |
| DK2931897T3 (en) * | 2012-12-12 | 2018-02-05 | Broad Inst Inc | CONSTRUCTION, MODIFICATION AND OPTIMIZATION OF SYSTEMS, PROCEDURES AND COMPOSITIONS FOR SEQUENCE MANIPULATION AND THERAPEUTICAL APPLICATIONS |
| MX2015017312A (es) * | 2013-06-17 | 2017-04-10 | Broad Inst Inc | Suministro y uso de composiciones, vectores y sistemas crispr-cas para la modificación dirigida y terapia hepáticas. |
| EP3245221A4 (en) * | 2015-01-16 | 2018-06-13 | Voyager Therapeutics, Inc. | Central nervous system targeting polynucleotides |
| KR102423442B1 (ko) * | 2015-12-11 | 2022-07-20 | 캘리포니아 인스티튜트 오브 테크놀로지 | 아데노-관련 바이러스를 지시하기 위한 타겟팅 펩타이드 |
| WO2017151884A1 (en) * | 2016-03-02 | 2017-09-08 | The Children's Hospital Of Philadelphia | Therapy for frontotemporal dementia |
| KR102709597B1 (ko) * | 2017-10-03 | 2024-09-26 | 프리베일 테라퓨틱스, 인크. | 리소좀 장애를 위한 유전자 요법 |
| IL274926B2 (en) * | 2017-12-01 | 2026-04-01 | Encoded Therapeutics Inc | Pyrazolopyrimidines with activity against respiratory syncytial virus |
| KR102171360B1 (ko) * | 2018-06-22 | 2020-10-28 | 재단법인대구경북과학기술원 | 사이토카인 융합 폴리펩티드, 및 이를 포함하는 사이토카인 라이브러리 |
| JP2022522995A (ja) * | 2019-01-18 | 2022-04-21 | ボイジャー セラピューティクス インコーポレイテッド | Ａａｖ粒子を生成するための方法及びシステム |
| BR112021015817A2 (pt) * | 2019-02-22 | 2021-10-13 | The Trustees Of The University Of Pennsylvania | Vírus adeno-associado recombinante para tratamento de neurodegeneração com início na idade adulta associado a grn |
| US12595479B2 (en) * | 2019-03-20 | 2026-04-07 | President And Fellows Of Harvard College | Antisense oligonucleotide-based progranulin augmentation therapy in neurodegenerative diseases |
-
2019
- 2019-09-27 GB GB201913974A patent/GB201913974D0/en not_active Ceased
-
2020
- 2020-09-28 CN CN202410972636.6A patent/CN119913208A/zh active Pending
- 2020-09-28 CN CN202080067598.XA patent/CN114450413B/zh active Active
- 2020-09-28 WO PCT/EP2020/077144 patent/WO2021058830A1/en not_active Ceased
- 2020-09-28 EP EP20781509.3A patent/EP4034664A1/en active Pending
- 2020-09-28 AU AU2020354538A patent/AU2020354538A1/en active Pending
- 2020-09-28 JP JP2022519283A patent/JP2022549892A/ja active Pending
- 2020-09-28 CA CA3155742A patent/CA3155742A1/en active Pending
- 2020-09-28 US US17/763,644 patent/US20220380804A1/en active Pending
- 2020-09-28 CN CN202410972634.7A patent/CN119753024A/zh active Pending
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