JPWO2019204303A5 - - Google Patents

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JPWO2019204303A5
JPWO2019204303A5 JP2020557155A JP2020557155A JPWO2019204303A5 JP WO2019204303 A5 JPWO2019204303 A5 JP WO2019204303A5 JP 2020557155 A JP2020557155 A JP 2020557155A JP 2020557155 A JP2020557155 A JP 2020557155A JP WO2019204303 A5 JPWO2019204303 A5 JP WO2019204303A5
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Japan
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triple
raav
spiral
dystrophin
helix
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JP2020557155A
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Japanese (ja)
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JP2021521782A5 (https=
JP7575273B2 (ja
JP2021521782A (ja
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Priority claimed from PCT/US2019/027675 external-priority patent/WO2019204303A2/en
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Publication of JPWO2019204303A5 publication Critical patent/JPWO2019204303A5/ja
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JP2020557155A 2018-04-16 2019-04-16 デュシェンヌ型筋ジストロフィーを治療するための組成物及び方法 Active JP7575273B2 (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201862658464P 2018-04-16 2018-04-16
US62/658,464 2018-04-16
PCT/US2019/027675 WO2019204303A2 (en) 2018-04-16 2019-04-16 Compositions and methods for treating duchenne muscular dystrophy

Publications (4)

Publication Number Publication Date
JP2021521782A JP2021521782A (ja) 2021-08-30
JP2021521782A5 JP2021521782A5 (https=) 2022-04-19
JPWO2019204303A5 true JPWO2019204303A5 (https=) 2022-04-19
JP7575273B2 JP7575273B2 (ja) 2024-10-29

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JP2020557155A Active JP7575273B2 (ja) 2018-04-16 2019-04-16 デュシェンヌ型筋ジストロフィーを治療するための組成物及び方法

Country Status (6)

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US (2) US12460226B2 (https=)
EP (1) EP3780952A4 (https=)
JP (1) JP7575273B2 (https=)
CN (1) CN112601454B (https=)
CA (1) CA3099958A1 (https=)
WO (1) WO2019204303A2 (https=)

Families Citing this family (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP3813871A4 (en) * 2018-06-29 2022-10-12 Icahn School of Medicine at Mount Sinai SPHINGOLIPID METABOLIZING PROTEINS ENCODING FOR ANC80
IL294713A (en) * 2020-01-16 2022-09-01 Takeda Pharmaceuticals Co Adeno associated virus based gene therapy for phenylketonuria
CN113999861B (zh) * 2021-09-08 2024-03-15 三峡大学 腺相关病毒衣壳蛋白保守区多克隆抗体的制备方法及应用

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