JPWO2019157056A5 - - Google Patents

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Publication number
JPWO2019157056A5
JPWO2019157056A5 JP2020542569A JP2020542569A JPWO2019157056A5 JP WO2019157056 A5 JPWO2019157056 A5 JP WO2019157056A5 JP 2020542569 A JP2020542569 A JP 2020542569A JP 2020542569 A JP2020542569 A JP 2020542569A JP WO2019157056 A5 JPWO2019157056 A5 JP WO2019157056A5
Authority
JP
Japan
Prior art keywords
formulation
migalastat
use according
salt
effective amount
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2020542569A
Other languages
English (en)
Japanese (ja)
Other versions
JP2021512896A (ja
JP2021512896A5 (https=
Publication date
Application filed filed Critical
Priority claimed from PCT/US2019/016853 external-priority patent/WO2019157056A1/en
Publication of JP2021512896A publication Critical patent/JP2021512896A/ja
Publication of JPWO2019157056A5 publication Critical patent/JPWO2019157056A5/ja
Publication of JP2021512896A5 publication Critical patent/JP2021512896A5/ja
Priority to JP2023192942A priority Critical patent/JP2024026080A/ja
Withdrawn legal-status Critical Current

Links

JP2020542569A 2018-02-06 2019-02-06 古典型ファブリー病患者の治療 Withdrawn JP2021512896A (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2023192942A JP2024026080A (ja) 2018-02-06 2023-11-13 古典型ファブリー病患者の治療

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201862626992P 2018-02-06 2018-02-06
US62/626,992 2018-02-06
PCT/US2019/016853 WO2019157056A1 (en) 2018-02-06 2019-02-06 Treatment of patients with classic fabry disease

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2023192942A Division JP2024026080A (ja) 2018-02-06 2023-11-13 古典型ファブリー病患者の治療

Publications (3)

Publication Number Publication Date
JP2021512896A JP2021512896A (ja) 2021-05-20
JPWO2019157056A5 true JPWO2019157056A5 (https=) 2023-06-06
JP2021512896A5 JP2021512896A5 (https=) 2023-06-06

Family

ID=65494622

Family Applications (2)

Application Number Title Priority Date Filing Date
JP2020542569A Withdrawn JP2021512896A (ja) 2018-02-06 2019-02-06 古典型ファブリー病患者の治療
JP2023192942A Pending JP2024026080A (ja) 2018-02-06 2023-11-13 古典型ファブリー病患者の治療

Family Applications After (1)

Application Number Title Priority Date Filing Date
JP2023192942A Pending JP2024026080A (ja) 2018-02-06 2023-11-13 古典型ファブリー病患者の治療

Country Status (20)

Country Link
US (1) US20210038579A1 (https=)
EP (2) EP4316589A3 (https=)
JP (2) JP2021512896A (https=)
KR (1) KR20200128675A (https=)
CN (1) CN112203657A (https=)
AR (1) AR114392A1 (https=)
AU (2) AU2019217603A1 (https=)
DK (1) DK3749308T3 (https=)
ES (1) ES2969263T3 (https=)
FI (1) FI3749308T3 (https=)
HR (1) HRP20240025T1 (https=)
HU (1) HUE064761T2 (https=)
LT (1) LT3749308T (https=)
PL (1) PL3749308T3 (https=)
PT (1) PT3749308T (https=)
RS (1) RS65103B1 (https=)
SI (1) SI3749308T1 (https=)
SM (1) SMT202400027T1 (https=)
TW (2) TWI869336B (https=)
WO (1) WO2019157056A1 (https=)

Families Citing this family (7)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
ES2573498T3 (es) 2006-05-16 2016-06-08 Amicus Therapeutics, Inc. Opciones de tratamiento para la enfermedad de Fabry
SI3470077T1 (sl) 2008-02-12 2020-12-31 Amicus Therapeutics, Inc. Postopek za napovedovanje odgovora na zdravljenje bolezni s farmakološkim spremljevalcem
CA3224537C (en) 2017-05-30 2025-09-09 Amicus Therapeutics, Inc. USE OF MIGALASTAT IN THE TREATMENT OF PATIENTS WITH FABRY DISEASE AND RENAL FAILURE
CA3090496C (en) 2018-02-06 2024-03-26 Amicus Therapeutics, Inc. Use of migalastat for treating fabry disease in pregnant patients
EP4282472A3 (en) 2018-08-20 2024-02-21 Amicus Therapeutics, Inc. Methods of treating fabry disease in patients having a mutation in the gla gene
EP3851105B1 (en) 2019-08-07 2026-03-04 Amicus Therapeutics, Inc. Migalastat for use in treating fabry disease in patients having a mutation in the gla gene
US11623916B2 (en) 2020-12-16 2023-04-11 Amicus Therapeutics, Inc. Highly purified batches of pharmaceutical grade migalastat and methods of producing the same

Family Cites Families (7)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US6274597B1 (en) 1998-06-01 2001-08-14 Mount Sinai School Of Medicine Of New York University Method of enhancing lysosomal α-Galactosidase A
ES2573498T3 (es) * 2006-05-16 2016-06-08 Amicus Therapeutics, Inc. Opciones de tratamiento para la enfermedad de Fabry
AU2008232614A1 (en) 2007-03-30 2008-10-09 Amicus Therapeutics, Inc. Method for the treatment of Fabry disease using pharmacological chaperones
SI3470077T1 (sl) 2008-02-12 2020-12-31 Amicus Therapeutics, Inc. Postopek za napovedovanje odgovora na zdravljenje bolezni s farmakološkim spremljevalcem
KR102004114B1 (ko) * 2016-03-22 2019-07-26 아미쿠스 세라퓨틱스, 인코포레이티드 Gla 유전자에 g9331a 돌연변이를 갖는 환자에서 파브리 질병의 치료 방법
AR109103A1 (es) 2016-07-19 2018-10-31 Amicus Therapeutics Inc Tratamiento de la enfermedad de fabry en pacientes no tratados y tratados previamente con ert
WO2019017938A1 (en) * 2017-07-19 2019-01-24 Amicus Therapeutics, Inc. TREATMENT OF FABRY'S DISEASE IN PATIENTS WITHOUT SUBSTITUTED ENZYMATIC THERAPY (TES) AND PATIENTS SUBJECT TO TES

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