JPWO2019046244A5 - - Google Patents
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- Publication number
- JPWO2019046244A5 JPWO2019046244A5 JP2020511971A JP2020511971A JPWO2019046244A5 JP WO2019046244 A5 JPWO2019046244 A5 JP WO2019046244A5 JP 2020511971 A JP2020511971 A JP 2020511971A JP 2020511971 A JP2020511971 A JP 2020511971A JP WO2019046244 A5 JPWO2019046244 A5 JP WO2019046244A5
- Authority
- JP
- Japan
- Prior art keywords
- migalastat
- salt
- formulation
- mwfs
- patient
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Granted
Links
Priority Applications (2)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2022203783A JP2023051998A (ja) | 2017-08-28 | 2022-12-20 | ファブリー病患者における心臓機能の強化及び/または安定化方法 |
| JP2025088523A JP2025138638A (ja) | 2017-08-28 | 2025-05-28 | ファブリー病患者における心臓機能の強化及び/または安定化方法 |
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201762550984P | 2017-08-28 | 2017-08-28 | |
| US62/550,984 | 2017-08-28 | ||
| PCT/US2018/048257 WO2019046244A1 (en) | 2017-08-28 | 2018-08-28 | METHODS FOR ENHANCING AND / OR STABILIZING CARDIAC FUNCTION IN PATIENTS WITH FABRY DISEASE |
Related Child Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022203783A Division JP2023051998A (ja) | 2017-08-28 | 2022-12-20 | ファブリー病患者における心臓機能の強化及び/または安定化方法 |
| JP2025088523A Division JP2025138638A (ja) | 2017-08-28 | 2025-05-28 | ファブリー病患者における心臓機能の強化及び/または安定化方法 |
Publications (4)
| Publication Number | Publication Date |
|---|---|
| JP2020531550A JP2020531550A (ja) | 2020-11-05 |
| JP2020531550A5 JP2020531550A5 (https=) | 2025-06-10 |
| JPWO2019046244A5 true JPWO2019046244A5 (https=) | 2025-06-10 |
| JP7755929B2 JP7755929B2 (ja) | 2025-10-17 |
Family
ID=63528948
Family Applications (3)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2020511971A Active JP7755929B2 (ja) | 2017-08-28 | 2018-08-28 | ファブリー病患者における心臓機能の強化及び/または安定化方法 |
| JP2022203783A Pending JP2023051998A (ja) | 2017-08-28 | 2022-12-20 | ファブリー病患者における心臓機能の強化及び/または安定化方法 |
| JP2025088523A Pending JP2025138638A (ja) | 2017-08-28 | 2025-05-28 | ファブリー病患者における心臓機能の強化及び/または安定化方法 |
Family Applications After (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022203783A Pending JP2023051998A (ja) | 2017-08-28 | 2022-12-20 | ファブリー病患者における心臓機能の強化及び/または安定化方法 |
| JP2025088523A Pending JP2025138638A (ja) | 2017-08-28 | 2025-05-28 | ファブリー病患者における心臓機能の強化及び/または安定化方法 |
Country Status (26)
| Country | Link |
|---|---|
| US (1) | US20200222377A1 (https=) |
| EP (3) | EP4588476A1 (https=) |
| JP (3) | JP7755929B2 (https=) |
| KR (2) | KR102790184B1 (https=) |
| CN (1) | CN111770753A (https=) |
| AR (1) | AR112482A1 (https=) |
| AU (2) | AU2018326364B2 (https=) |
| CA (1) | CA3074450C (https=) |
| CL (1) | CL2020000491A1 (https=) |
| DK (2) | DK3675853T3 (https=) |
| EA (1) | EA202090564A1 (https=) |
| ES (2) | ES2931054T3 (https=) |
| FI (1) | FI4176877T3 (https=) |
| HR (2) | HRP20250064T1 (https=) |
| HU (2) | HUE060287T2 (https=) |
| IL (3) | IL272893B2 (https=) |
| LT (2) | LT4176877T (https=) |
| MX (2) | MX2020002229A (https=) |
| PL (2) | PL4176877T3 (https=) |
| PT (2) | PT4176877T (https=) |
| RS (2) | RS66515B1 (https=) |
| SG (1) | SG11202001707PA (https=) |
| SI (1) | SI4176877T1 (https=) |
| SM (2) | SMT202200459T1 (https=) |
| TW (1) | TWI845479B (https=) |
| WO (1) | WO2019046244A1 (https=) |
Families Citing this family (10)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| ES2573498T3 (es) | 2006-05-16 | 2016-06-08 | Amicus Therapeutics, Inc. | Opciones de tratamiento para la enfermedad de Fabry |
| SI3470077T1 (sl) | 2008-02-12 | 2020-12-31 | Amicus Therapeutics, Inc. | Postopek za napovedovanje odgovora na zdravljenje bolezni s farmakološkim spremljevalcem |
| CA3224537C (en) | 2017-05-30 | 2025-09-09 | Amicus Therapeutics, Inc. | USE OF MIGALASTAT IN THE TREATMENT OF PATIENTS WITH FABRY DISEASE AND RENAL FAILURE |
| IL272893B2 (en) | 2017-08-28 | 2024-07-01 | Amicus Therapeutics Inc | Methods of enhancing and/or stabilizing cardiac function in patients with fabry disease |
| CA3090496C (en) | 2018-02-06 | 2024-03-26 | Amicus Therapeutics, Inc. | Use of migalastat for treating fabry disease in pregnant patients |
| EP4282472A3 (en) | 2018-08-20 | 2024-02-21 | Amicus Therapeutics, Inc. | Methods of treating fabry disease in patients having a mutation in the gla gene |
| EP3851105B1 (en) | 2019-08-07 | 2026-03-04 | Amicus Therapeutics, Inc. | Migalastat for use in treating fabry disease in patients having a mutation in the gla gene |
| US11623916B2 (en) | 2020-12-16 | 2023-04-11 | Amicus Therapeutics, Inc. | Highly purified batches of pharmaceutical grade migalastat and methods of producing the same |
| TR2024011149A1 (tr) | 2024-08-23 | 2026-03-23 | Sanovel İlaç Sanayi̇ Ve Ti̇caret Anoni̇m Şi̇rketi̇ | Mi̇galastat i̇çeren kapsül formülasyonlari |
| CN119120696A (zh) * | 2024-11-12 | 2024-12-13 | 北京贝瑞和康生物技术有限公司 | 检测法布雷病gla基因突变的引物组、试剂盒及其应用 |
Family Cites Families (6)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US6274597B1 (en) | 1998-06-01 | 2001-08-14 | Mount Sinai School Of Medicine Of New York University | Method of enhancing lysosomal α-Galactosidase A |
| AU2008232614A1 (en) | 2007-03-30 | 2008-10-09 | Amicus Therapeutics, Inc. | Method for the treatment of Fabry disease using pharmacological chaperones |
| US9999618B2 (en) * | 2007-04-26 | 2018-06-19 | Amicus Therapeutics, Inc. | Dosing regimens for the treatment of lysosomal storage diseases using pharmacological chaperones |
| SI3470077T1 (sl) | 2008-02-12 | 2020-12-31 | Amicus Therapeutics, Inc. | Postopek za napovedovanje odgovora na zdravljenje bolezni s farmakološkim spremljevalcem |
| IL272893B2 (en) | 2017-08-28 | 2024-07-01 | Amicus Therapeutics Inc | Methods of enhancing and/or stabilizing cardiac function in patients with fabry disease |
| CN111344912B (zh) | 2017-08-28 | 2021-12-28 | 约翰·梅扎林瓜联合股份有限公司 | 同轴电缆连接器的天气防护壳体 |
-
2018
- 2018-08-28 IL IL272893A patent/IL272893B2/en unknown
- 2018-08-28 SI SI201831201T patent/SI4176877T1/sl unknown
- 2018-08-28 DK DK18766482.6T patent/DK3675853T3/da active
- 2018-08-28 MX MX2020002229A patent/MX2020002229A/es unknown
- 2018-08-28 FI FIEP22194251.9T patent/FI4176877T3/fi active
- 2018-08-28 TW TW107129901A patent/TWI845479B/zh active
- 2018-08-28 KR KR1020207008736A patent/KR102790184B1/ko active Active
- 2018-08-28 PL PL22194251.9T patent/PL4176877T3/pl unknown
- 2018-08-28 EP EP24217100.7A patent/EP4588476A1/en active Pending
- 2018-08-28 CN CN201880056413.8A patent/CN111770753A/zh active Pending
- 2018-08-28 RS RS20250161A patent/RS66515B1/sr unknown
- 2018-08-28 IL IL310648A patent/IL310648A/en unknown
- 2018-08-28 PT PT221942519T patent/PT4176877T/pt unknown
- 2018-08-28 EP EP18766482.6A patent/EP3675853B1/en active Active
- 2018-08-28 RS RS20221061A patent/RS63742B1/sr unknown
- 2018-08-28 AU AU2018326364A patent/AU2018326364B2/en active Active
- 2018-08-28 LT LTEP22194251.9T patent/LT4176877T/lt unknown
- 2018-08-28 SG SG11202001707PA patent/SG11202001707PA/en unknown
- 2018-08-28 JP JP2020511971A patent/JP7755929B2/ja active Active
- 2018-08-28 SM SM20220459T patent/SMT202200459T1/it unknown
- 2018-08-28 US US16/642,620 patent/US20200222377A1/en active Pending
- 2018-08-28 DK DK22194251.9T patent/DK4176877T3/da active
- 2018-08-28 PL PL18766482.6T patent/PL3675853T3/pl unknown
- 2018-08-28 WO PCT/US2018/048257 patent/WO2019046244A1/en not_active Ceased
- 2018-08-28 HR HRP20250064TT patent/HRP20250064T1/hr unknown
- 2018-08-28 EP EP22194251.9A patent/EP4176877B1/en active Active
- 2018-08-28 HU HUE18766482A patent/HUE060287T2/hu unknown
- 2018-08-28 ES ES18766482T patent/ES2931054T3/es active Active
- 2018-08-28 HU HUE22194251A patent/HUE070433T2/hu unknown
- 2018-08-28 AR ARP180102438 patent/AR112482A1/es unknown
- 2018-08-28 LT LTEPPCT/US2018/048257T patent/LT3675853T/lt unknown
- 2018-08-28 SM SM20250073T patent/SMT202500073T1/it unknown
- 2018-08-28 PT PT187664826T patent/PT3675853T/pt unknown
- 2018-08-28 KR KR1020257010249A patent/KR20250049561A/ko active Pending
- 2018-08-28 HR HRP20221366TT patent/HRP20221366T1/hr unknown
- 2018-08-28 CA CA3074450A patent/CA3074450C/en active Active
- 2018-08-28 ES ES22194251T patent/ES3013820T3/es active Active
- 2018-08-28 EA EA202090564A patent/EA202090564A1/ru unknown
-
2020
- 2020-02-27 MX MX2023005628A patent/MX2023005628A/es unknown
- 2020-02-28 CL CL2020000491A patent/CL2020000491A1/es unknown
-
2022
- 2022-12-20 JP JP2022203783A patent/JP2023051998A/ja active Pending
-
2024
- 2024-11-27 AU AU2024266945A patent/AU2024266945A1/en active Pending
-
2025
- 2025-05-28 JP JP2025088523A patent/JP2025138638A/ja active Pending
- 2025-10-23 IL IL324182A patent/IL324182A/en unknown
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