JPWO2019046244A5 - - Google Patents

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Publication number
JPWO2019046244A5
JPWO2019046244A5 JP2020511971A JP2020511971A JPWO2019046244A5 JP WO2019046244 A5 JPWO2019046244 A5 JP WO2019046244A5 JP 2020511971 A JP2020511971 A JP 2020511971A JP 2020511971 A JP2020511971 A JP 2020511971A JP WO2019046244 A5 JPWO2019046244 A5 JP WO2019046244A5
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JP
Japan
Prior art keywords
migalastat
salt
formulation
mwfs
patient
Prior art date
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Application number
JP2020511971A
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English (en)
Japanese (ja)
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JP2020531550A5 (https=
JP2020531550A (ja
JP7755929B2 (ja
Publication date
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Priority claimed from PCT/US2018/048257 external-priority patent/WO2019046244A1/en
Publication of JP2020531550A publication Critical patent/JP2020531550A/ja
Priority to JP2022203783A priority Critical patent/JP2023051998A/ja
Priority to JP2025088523A priority patent/JP2025138638A/ja
Publication of JP2020531550A5 publication Critical patent/JP2020531550A5/ja
Publication of JPWO2019046244A5 publication Critical patent/JPWO2019046244A5/ja
Application granted granted Critical
Publication of JP7755929B2 publication Critical patent/JP7755929B2/ja
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JP2020511971A 2017-08-28 2018-08-28 ファブリー病患者における心臓機能の強化及び/または安定化方法 Active JP7755929B2 (ja)

Priority Applications (2)

Application Number Priority Date Filing Date Title
JP2022203783A JP2023051998A (ja) 2017-08-28 2022-12-20 ファブリー病患者における心臓機能の強化及び/または安定化方法
JP2025088523A JP2025138638A (ja) 2017-08-28 2025-05-28 ファブリー病患者における心臓機能の強化及び/または安定化方法

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201762550984P 2017-08-28 2017-08-28
US62/550,984 2017-08-28
PCT/US2018/048257 WO2019046244A1 (en) 2017-08-28 2018-08-28 METHODS FOR ENHANCING AND / OR STABILIZING CARDIAC FUNCTION IN PATIENTS WITH FABRY DISEASE

Related Child Applications (2)

Application Number Title Priority Date Filing Date
JP2022203783A Division JP2023051998A (ja) 2017-08-28 2022-12-20 ファブリー病患者における心臓機能の強化及び/または安定化方法
JP2025088523A Division JP2025138638A (ja) 2017-08-28 2025-05-28 ファブリー病患者における心臓機能の強化及び/または安定化方法

Publications (4)

Publication Number Publication Date
JP2020531550A JP2020531550A (ja) 2020-11-05
JP2020531550A5 JP2020531550A5 (https=) 2025-06-10
JPWO2019046244A5 true JPWO2019046244A5 (https=) 2025-06-10
JP7755929B2 JP7755929B2 (ja) 2025-10-17

Family

ID=63528948

Family Applications (3)

Application Number Title Priority Date Filing Date
JP2020511971A Active JP7755929B2 (ja) 2017-08-28 2018-08-28 ファブリー病患者における心臓機能の強化及び/または安定化方法
JP2022203783A Pending JP2023051998A (ja) 2017-08-28 2022-12-20 ファブリー病患者における心臓機能の強化及び/または安定化方法
JP2025088523A Pending JP2025138638A (ja) 2017-08-28 2025-05-28 ファブリー病患者における心臓機能の強化及び/または安定化方法

Family Applications After (2)

Application Number Title Priority Date Filing Date
JP2022203783A Pending JP2023051998A (ja) 2017-08-28 2022-12-20 ファブリー病患者における心臓機能の強化及び/または安定化方法
JP2025088523A Pending JP2025138638A (ja) 2017-08-28 2025-05-28 ファブリー病患者における心臓機能の強化及び/または安定化方法

Country Status (26)

Country Link
US (1) US20200222377A1 (https=)
EP (3) EP4588476A1 (https=)
JP (3) JP7755929B2 (https=)
KR (2) KR102790184B1 (https=)
CN (1) CN111770753A (https=)
AR (1) AR112482A1 (https=)
AU (2) AU2018326364B2 (https=)
CA (1) CA3074450C (https=)
CL (1) CL2020000491A1 (https=)
DK (2) DK3675853T3 (https=)
EA (1) EA202090564A1 (https=)
ES (2) ES2931054T3 (https=)
FI (1) FI4176877T3 (https=)
HR (2) HRP20250064T1 (https=)
HU (2) HUE060287T2 (https=)
IL (3) IL272893B2 (https=)
LT (2) LT4176877T (https=)
MX (2) MX2020002229A (https=)
PL (2) PL4176877T3 (https=)
PT (2) PT4176877T (https=)
RS (2) RS66515B1 (https=)
SG (1) SG11202001707PA (https=)
SI (1) SI4176877T1 (https=)
SM (2) SMT202200459T1 (https=)
TW (1) TWI845479B (https=)
WO (1) WO2019046244A1 (https=)

Families Citing this family (10)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
ES2573498T3 (es) 2006-05-16 2016-06-08 Amicus Therapeutics, Inc. Opciones de tratamiento para la enfermedad de Fabry
SI3470077T1 (sl) 2008-02-12 2020-12-31 Amicus Therapeutics, Inc. Postopek za napovedovanje odgovora na zdravljenje bolezni s farmakološkim spremljevalcem
CA3224537C (en) 2017-05-30 2025-09-09 Amicus Therapeutics, Inc. USE OF MIGALASTAT IN THE TREATMENT OF PATIENTS WITH FABRY DISEASE AND RENAL FAILURE
IL272893B2 (en) 2017-08-28 2024-07-01 Amicus Therapeutics Inc Methods of enhancing and/or stabilizing cardiac function in patients with fabry disease
CA3090496C (en) 2018-02-06 2024-03-26 Amicus Therapeutics, Inc. Use of migalastat for treating fabry disease in pregnant patients
EP4282472A3 (en) 2018-08-20 2024-02-21 Amicus Therapeutics, Inc. Methods of treating fabry disease in patients having a mutation in the gla gene
EP3851105B1 (en) 2019-08-07 2026-03-04 Amicus Therapeutics, Inc. Migalastat for use in treating fabry disease in patients having a mutation in the gla gene
US11623916B2 (en) 2020-12-16 2023-04-11 Amicus Therapeutics, Inc. Highly purified batches of pharmaceutical grade migalastat and methods of producing the same
TR2024011149A1 (tr) 2024-08-23 2026-03-23 Sanovel İlaç Sanayi̇ Ve Ti̇caret Anoni̇m Şi̇rketi̇ Mi̇galastat i̇çeren kapsül formülasyonlari
CN119120696A (zh) * 2024-11-12 2024-12-13 北京贝瑞和康生物技术有限公司 检测法布雷病gla基因突变的引物组、试剂盒及其应用

Family Cites Families (6)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US6274597B1 (en) 1998-06-01 2001-08-14 Mount Sinai School Of Medicine Of New York University Method of enhancing lysosomal α-Galactosidase A
AU2008232614A1 (en) 2007-03-30 2008-10-09 Amicus Therapeutics, Inc. Method for the treatment of Fabry disease using pharmacological chaperones
US9999618B2 (en) * 2007-04-26 2018-06-19 Amicus Therapeutics, Inc. Dosing regimens for the treatment of lysosomal storage diseases using pharmacological chaperones
SI3470077T1 (sl) 2008-02-12 2020-12-31 Amicus Therapeutics, Inc. Postopek za napovedovanje odgovora na zdravljenje bolezni s farmakološkim spremljevalcem
IL272893B2 (en) 2017-08-28 2024-07-01 Amicus Therapeutics Inc Methods of enhancing and/or stabilizing cardiac function in patients with fabry disease
CN111344912B (zh) 2017-08-28 2021-12-28 约翰·梅扎林瓜联合股份有限公司 同轴电缆连接器的天气防护壳体

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