IL294625A - Treatment of mucopolysaccharidosis i with human fully glycosylated human alpha-l-iduronidase (idua) - Google Patents
Treatment of mucopolysaccharidosis i with human fully glycosylated human alpha-l-iduronidase (idua)Info
- Publication number
- IL294625A IL294625A IL294625A IL29462522A IL294625A IL 294625 A IL294625 A IL 294625A IL 294625 A IL294625 A IL 294625A IL 29462522 A IL29462522 A IL 29462522A IL 294625 A IL294625 A IL 294625A
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- Israel
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- human
- dose
- certain embodiments
- brain
- administered
- Prior art date
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| PCT/US2021/014129 WO2021150570A1 (en) | 2020-01-22 | 2021-01-20 | Treatment of mucopolysaccharidosis i with fully-human glycosylated human alpha-l-iduronidase (idua) |
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| IL294625A IL294625A (en) | 2020-01-22 | 2021-01-20 | Treatment of mucopolysaccharidosis i with human fully glycosylated human alpha-l-iduronidase (idua) |
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| TWI835747B (zh) | 2017-09-22 | 2024-03-21 | 賓州大學委員會 | 用於治療黏多醣病 ii 型之基因治療 |
| CA3167741A1 (en) * | 2020-01-29 | 2021-08-05 | Regenxbio Inc. | Treatment of mucopolysaccharidosis ii with recombinant human iduronate-2-sulfatase (ids) produced by human neural or glial cells |
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| NZ532635A (en) | 2001-11-13 | 2007-05-31 | Univ Pennsylvania | A method of identifying unknown adeno-associated virus (AAV) sequences and a kit for the method |
| DK2359869T3 (en) | 2001-12-17 | 2019-04-15 | Univ Pennsylvania | Sequences of adeno-associated virus (AAV) serotype 8, vectors containing these, and uses thereof |
| CN1856576B (zh) | 2003-09-30 | 2011-05-04 | 宾夕法尼亚州立大学托管会 | 腺伴随病毒(aav)进化支、序列、含有这些序列的载体及它们的应用 |
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| HUE052676T2 (hu) | 2013-10-11 | 2021-05-28 | Massachusetts Eye & Ear Infirmary | Eljárások õsi vírusszekvenciák elõrejelzésére és alkalmazásaik |
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| JP7042814B2 (ja) * | 2016-11-01 | 2022-03-28 | 日本光電工業株式会社 | 患者の頭部に配置されて当該患者の脳の皮質組織の脈動を測定するためのトランスデューサを含むシステム |
| EP3541946A1 (en) * | 2016-11-15 | 2019-09-25 | Regents Of The University Of Minnesota | Method for improving neurological function in mpsi and mpsii and other neurological disorders |
| CA3049915A1 (en) * | 2017-01-31 | 2018-08-09 | Stephen YOO | Treatment of mucopolysaccharidosis i with fully-human glycosylated human alpha-l-iduronidase (idua) |
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| JP2023511382A (ja) | 2023-03-17 |
| AU2021211416A1 (en) | 2022-08-11 |
| BR112022014563A2 (pt) | 2022-09-13 |
| WO2021150570A1 (en) | 2021-07-29 |
| US20230059395A1 (en) | 2023-02-23 |
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