CN113005123A - 用于神经变性疾病的基因疗法 - Google Patents

用于神经变性疾病的基因疗法 Download PDF

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CN113005123A
CN113005123A CN202110196181.XA CN202110196181A CN113005123A CN 113005123 A CN113005123 A CN 113005123A CN 202110196181 A CN202110196181 A CN 202110196181A CN 113005123 A CN113005123 A CN 113005123A
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nucleic acid
ser
pro
raav
vector
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阿萨·阿贝利奥维奇
劳拉·赫克曼
赫维·莱茵
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Privelle Therapeutics
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Privelle Therapeutics
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CN202110196181.XA 2017-10-23 2018-10-23 用于神经变性疾病的基因疗法 Pending CN113005123A (zh)

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US201762575795P 2017-10-23 2017-10-23
US62/575,795 2017-10-23
US201862742723P 2018-10-08 2018-10-08
US62/742,723 2018-10-08
CN201880081355.4A CN111819281B (zh) 2017-10-23 2018-10-23 用于神经变性疾病的基因疗法

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US (1) US20210261981A1 (https=)
EP (1) EP3701030A4 (https=)
JP (2) JP7413256B2 (https=)
KR (1) KR20200075865A (https=)
CN (2) CN113005123A (https=)
AU (1) AU2018354195A1 (https=)
BR (1) BR112020008033A2 (https=)
CA (2) CA3177979A1 (https=)
IL (2) IL274129A (https=)
MX (1) MX2020004207A (https=)
WO (1) WO2019084068A1 (https=)

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KR20230088393A (ko) 2020-10-15 2023-06-19 프리베일 테라퓨틱스, 인크. 재조합 아데노 연관 바이러스 조성물 및 이의 제조 방법
US20240044869A1 (en) 2020-10-15 2024-02-08 Prevail Therapeutics, Inc. Assay for measuring potency of gene therapy drug product
EP4252846A4 (en) 2020-11-06 2025-12-03 Sumitomo Pharma Co Ltd REGULATOR FOR THE EXPRESSION AND/OR FUNCTION OF THE RPS25 GENE
WO2022164260A1 (ko) 2021-01-28 2022-08-04 주식회사 에이브레인 신경 퇴행성 질환의 치료를 위한 유전자 요법
CN117043179A (zh) 2021-01-28 2023-11-10 爱博瑞株式会社 用于治疗神经退行性疾病的基因治疗
KR102707250B1 (ko) 2021-10-28 2024-09-13 한국해양과학기술원 신규 화합물 및 이를 유효성분으로 포함하는 신경염증성 뇌질환 예방 또는 치료용 조성물
AR128239A1 (es) * 2022-01-10 2024-04-10 Univ Pennsylvania Composiciones y métodos útiles para el tratamiento de trastornos mediados por c9orf72
TW202511485A (zh) 2023-06-16 2025-03-16 日商住友製藥股份有限公司 調節ｒｐｓ２５基因之表現及／或其功能的反義寡核苷酸

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KR20200075865A (ko) 2020-06-26
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